<i>N</i>-Substituted <scp>l</scp>-Iminosugars for the Treatment of Sanfilippo Type B Syndrome-Reference-Cited by-同舟云学术

N-Substituted l-Iminosugars for the Treatment of Sanfilippo Type B Syndrome

Published:2023-01-25 Issue:3 Volume:66 Page:1790-1808
ISSN:0022-2623
Container-title:Journal of Medicinal Chemistry
language:en
Short-container-title:J. Med. Chem.

Author:

De Pasquale Valeria¹,Esposito Anna²^ORCID,Scerra Gianluca³,Scarcella Melania³,Ciampa Mariangela³,Luongo Antonietta⁴,D’Alonzo Daniele⁵^ORCID,Guaragna Annalisa²^ORCID,D’Agostino Massimo³,Pavone Luigi Michele³^ORCID

Affiliation:

1. Department of Veterinary Medicine and Animal Productions, University of Naples Federico II, Via F. Delpino 1, 80137 Naples, Italy

2. Department of Chemical, Materials and Production Engineering, University of Naples Federico II, Piazzale V. Tecchio 80, 80125 Naples, Italy

3. Department of Molecular Medicine and Medical Biotechnology, University of Naples Federico II, Via S. Pansini 5, 80131 Naples, Italy

4. AORN Sant’Anna e San Sebastiano, Via F. Palasciano, 81100 Caserta, Italy

5. Department of Chemical Sciences, University of Naples Federico II, Via Cintia, 80126 Napoli, Italy

Funder

Cure Sanfilippo Foundation

Publisher

American Chemical Society (ACS)

Subject

Drug Discovery,Molecular Medicine

Link

https://pubs.acs.org/doi/pdf/10.1021/acs.jmedchem.2c01617

Reference88 articles.

1. Molecular Bases of Neurodegeneration and Cognitive Decline, the Major Burden of Sanfilippo Disease

2. Overview of the mucopolysaccharidoses

3. A Cure for Sanfilippo Syndrome? A Summary of Current Therapeutic Approaches and their Promise

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