Spacer Fidelity Assessments of Guide RNA by Top-Down Mass Spectrometry-Reference-Cited by-同舟云学术

Spacer Fidelity Assessments of Guide RNA by Top-Down Mass Spectrometry

Published:2023-07-11 Issue:7 Volume:9 Page:1437-1452
ISSN:2374-7943
Container-title:ACS Central Science
language:en
Short-container-title:ACS Cent. Sci.

Author:

Macias Luis A.¹^ORCID,Garcia Sara P.¹,Back Kayla M.¹,Wu Yue¹,Johnson G. Hall²,Kathiresan Sekar¹,Bellinger Andrew M.¹,Rohde Ellen¹,Freitas Michael A.²³^ORCID,Madsen James A.¹^ORCID

Affiliation:

1. Verve Therapeutics, 201 Brookline Avenue, Suite 601, Boston, Massachusetts 02215, United States

2. MassMatrix, Inc., 600 Teteridge Road, Columbus, Ohio 43214, United States

3. The Ohio State University, 281 West Lane Avenue, Columbus, Ohio 43210, United States

Funder

Verve Therapeutics

Publisher

American Chemical Society (ACS)

Subject

General Chemical Engineering,General Chemistry

Link

https://pubs.acs.org/doi/pdf/10.1021/acscentsci.3c00289

Reference63 articles.

1. In vivo CRISPR base editing of PCSK9 durably lowers cholesterol in primates

2. GalNAc-Lipid nanoparticles enable non-LDLR dependent hepatic delivery of a CRISPR base editing therapy

3. Global, regional, and national age-sex-specific mortality for 282 causes of death in 195 countries and territories, 1980–2017: a systematic analysis for the Global Burden of Disease Study 2017

4. CRISPR-Cas9 In Vivo Gene Editing for Transthyretin Amyloidosis

5. A Programmable Dual-RNA–Guided DNA Endonuclease in Adaptive Bacterial Immunity

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