Therapy of X-linked adrenoleukodystrophy: Prognosis based upon age and MRI abnormality and plans for placebo-controlled trials-Reference-Cited by-同舟云学术

Therapy of X-linked adrenoleukodystrophy: Prognosis based upon age and MRI abnormality and plans for placebo-controlled trials

Published:2000-05 Issue:3 Volume:23 Page:273-277
ISSN:0141-8955
Container-title:Journal of Inherited Metabolic Disease
language:en
Short-container-title:J Inherit Metab Dis

Author:

Moser H. W.¹,Bezman L.¹,Lu S. E.¹,Raymond G. V.¹

Affiliation:

1. ; Kennedy Krieger Institute and the Departments of Neurology and Pediatrics; Johns Hopkins University and the Department of Biostatistics, School of Public Health; 707 North Broadway Baltimore MD 21205 USA

Publisher

Wiley

Subject

Genetics(clinical),Genetics

Link

http://onlinelibrary.wiley.com/wol1/doi/10.1023/A:1005688130338/fullpdf

Reference13 articles.

1. The incidence of X-linked adrenoleukodystrophy and the relativefrequency of its phenotypes;Bezman;Am J Med Genet,1998

2. Gene redundancy and pharmacological gene therapy: potential for X-linked adrenoleukodystrophy;Kemp;Nature Medicine,1998

3. The future for treatment by bone marrow transplantation for adrenoleukodystrophy, metachromatic leukodystrophy, globoid cell leukodystrophy and Hurler syndrome;Krivit;J Inherit Metab Dis,1995

4. Multisliceproton MR spectroscopic imaging in X-linked adrenoleukodystrophy;Kruse;Ann Neurol,1994

5. Adrenoleukodystrophy: a scoring method for brain MR observation;Loes;Am J Neuroradiol,1994

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