Successful allogeneic unrelated bone marrow transplantation using reduced-intensity conditioning for the treatment of X-linked adrenoleukodystrophy in a one-yr-old boy-Reference-Cited by-同舟云学术

Successful allogeneic unrelated bone marrow transplantation using reduced-intensity conditioning for the treatment of X-linked adrenoleukodystrophy in a one-yr-old boy

Published:2009-02 Issue:1 Volume:13 Page:130-133
ISSN:1397-3142
Container-title:Pediatric Transplantation
language:en
Short-container-title:

Author:

Okamura Kazumi,Watanabe Tsutomu,Onishi Toshihiro,Watanabe Hiroyoshi,Fujii Emiko,Mori Kenji,Matsuda Junko

Publisher

Wiley

Subject

Transplantation,Pediatrics, Perinatology and Child Health

Link

http://onlinelibrary.wiley.com/wol1/doi/10.1111/j.1399-3046.2008.00962.x/fullpdf

Reference18 articles.

1. X-linked adrenoleukodystrophy: The role of contrast-enhanced MR imaging in predicting disease progression;Melhem;Am J Neuroradiol,2000

2. Trends in haematopoietic cell transplantation for inborn errors of metabolism;Jan Boelens;J Inherit Metab Dis,2006

3. Cholesterol regulates ABCD2 expression: Implications for the therapy X-linked adrenoleukodystrophy;Weinhofer;Hum Mol Genet,2002

4. Phenyl butyrate up-regulates the adrenoleukodystrophy-related gene as a non-classical peroxisome proliferator;Gondcaille;J Cell Biol,2005

5. N-acetyl-L-cysteine improves the outcome of advanced cerebral adrenoleukodystrophy;Tolar;Bone Marrow Transplant,2007

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