Pompe disease: further challenges to pursue
Author:
Publisher
FapUNIFESP (SciELO)
Subject
Neurology,Neurology (clinical)
Link
http://www.scielo.br/pdf/anp/v71n5/0004-282X-anp-71-05-273.pdf
Reference16 articles.
1. Later-onset Pompe disease: early detection and early treatment initiation enabled by new born screening;Chien YH;J Pediatr,2011
2. Cross-reactive immunologic material status affects treatment outcomes in Pompe disease infants;Kishnani PS;Mol Genet Metab,2010
3. Long-term intravenous treatment of Pompe disease with recombinant human alpha-glucosidase from milk;Van den Hout JM;Pediatrics,2004
4. Enzyme replacement therapy in late-onset Pompe's disease: a three-year follow-up;Winkel LPF;Ann Neurol,2004
5. Elimination of antibodies to recombinant enzyme in Pompe's disease;Mendelsohn NJ;N Engl J Med,2009
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1. Late-Onset Glycogen Storage Disease Type 2;Current Molecular Medicine;2014-10-13
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