Enzyme replacement therapy in late-onset Pompe's disease: A three-year follow-up-Reference-Cited by-同舟云学术

Enzyme replacement therapy in late-onset Pompe's disease: A three-year follow-up

Published:2004 Issue:4 Volume:55 Page:495-502
ISSN:0364-5134
Container-title:Annals of Neurology
language:en
Short-container-title:Ann Neurol.

Author:

Winkel L�on P. F.,Van den Hout Johanna M. P.,Kamphoven Joep H. J.,Disseldorp Janus A. M.,Remmerswaal Maaike,Arts Willem F. M.,Loonen M. Christa B.,Vulto Arnold G.,Van Doorn Pieter A.,De Jong Gerard,Hop Wim,Smit G. Peter A.,Shapira Stuart K.,Boer Marijke A.,Reuser Arnold J. J.,Van der Ploeg Ans T.,van Diggelen Otto P.

Publisher

Wiley

Subject

Neurology (clinical),Neurology

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2. Myology;Engel,1994

3. The Natural Course of Infantile Pompe’s Disease: 20 Original Cases Compared With 133 Cases From the Literature

4. Recombinant human α-glucosidase from rabbit milk in Pompe patients

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