Seven‐year safety and efficacy with velaglucerase alfa for treatment‐naïve adult patients with type 1 G aucher disease
Author:
Affiliation:
1. Shaare Zedek Medical Center, affiliated with the Hebrew University‐Hadassah Medical SchoolJerusalem Israel
2. Shire, Lexington Massachusetts
Funder
Shire
Publisher
Wiley
Subject
Hematology
Link
https://onlinelibrary.wiley.com/doi/pdf/10.1002/ajh.24040
Reference22 articles.
1. Characterization of gene-activated human acid- -glucosidase: Crystal structure, glycan composition, and internalization into macrophages
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3. Velaglucerase alfa enzyme replacement therapy compared with imiglucerase in patients with Gaucher disease
4. Enzyme replacement therapy with velaglucerase alfa in Gaucher disease: Results from a randomized, double-blind, multinational, Phase 3 study
5. Safety and efficacy of velaglucerase alfa in Gaucher disease type 1 patients previously treated with imiglucerase
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1. A Real-World Investigation of MRI Changes in Bone in Patients with Type 1 Gaucher Disease Treated with Velaglucerase Alfa: The EIROS Study;Journal of Clinical Medicine;2024-05-16
2. Long-Term Treatment of Gaucher Disease with Velaglucerase Alfa in ERT-Naïve Patients from the Gaucher Outcome Survey (GOS) Registry;Journal of Clinical Medicine;2024-05-09
3. A retrospective and prospective observational study of MRI changes in bone in patients with type 1 Gaucher disease treated with velaglucerase alfa: the EIROS study.;2024-02-12
4. Gaucher Disease;Lysosomal Storage Disorders;2022-07-21
5. A Systematic Review and Meta-analyses of Longitudinal Studies on Drug Treatments for Gaucher Disease;Annals of Pharmacotherapy;2022-07-11
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