Enzyme replacement therapy with velaglucerase alfa in Gaucher disease: Results from a randomized, double-blind, multinational, Phase 3 study-Reference-Cited by-同舟云学术

Enzyme replacement therapy with velaglucerase alfa in Gaucher disease: Results from a randomized, double-blind, multinational, Phase 3 study

Published:2013-02-06 Issue:3 Volume:88 Page:166-171
ISSN:0361-8609
Container-title:American Journal of Hematology
language:en
Short-container-title:Am. J. Hematol.

Author:

Gonzalez Derlis E.¹,Turkia Hadhami Ben²,Lukina Elena A.³,Kisinovsky Isaac⁴,Dridi Marie-Françoise Ben²,Elstein Deborah⁵,Zahrieh David⁶,Crombez Eric⁶,Bhirangi Kiran⁶,Barton Norman W.⁶,Zimran Ari⁵

Affiliation:

1. Sanatorio Español; Asunción; Paraguay

2. La Rabta Hospital; Tunis; Tunisia

3. Hematology Research Center; Moscow; Russia

4. Your Health S. A.; BuenosAires; Argentina

5. Shaare Zedek Medical Center and Hebrew University-Hadassah Medical School; Jerusalem; Israel

6. Shire Human Genetic Therapies, Inc.; Lexington; Massachusetts

Publisher

Wiley

Subject

Hematology

Link

http://onlinelibrary.wiley.com/wol1/doi/10.1002/ajh.23381/fullpdf

Reference22 articles.

1. Gaucher's disease: Clinical features and natural history;Cox;Baillieres Clin Haematol,1997

2. Enzyme therapy in type 1 Gaucher disease: Comparative efficacy of mannose-terminated glucocerebrosidase from natural and recombinant sources;Grabowski;Ann Intern Med,1995

3. Replacement therapy with imiglucerase for type 1 Gaucher's disease;Zimran;Lancet,1995

4. Characterization of gene-activated human acid-β-glucosidase: Crystal structure, glycan composition, and internalization into macrophages;Brumshtein;Glycobiology,2010

Cited by 65 articles. 订阅此论文施引文献订阅此论文施引文献，注册后可以免费订阅5篇论文的施引文献，订阅后可以查看论文全部施引文献

1. Twelve Years of the Gaucher Outcomes Survey (GOS): Insights, Achievements, and Lessons Learned from a Global Patient Registry;Journal of Clinical Medicine;2024-06-19

2. Long-Term Treatment of Gaucher Disease with Velaglucerase Alfa in ERT-Naïve Patients from the Gaucher Outcome Survey (GOS) Registry;Journal of Clinical Medicine;2024-05-09

3. Assessing the diagnostic utility of the Gaucher Earlier Diagnosis Consensus (GED-C) scoring system using real-world data;Orphanet Journal of Rare Diseases;2024-02-16

4. Velaglucerase alfa for treatment in children with Gaucher disease type 1: the Russian experience;Pediatric Hematology/Oncology and Immunopathology;2023-10-01

5. Osteonecrosis in Gaucher disease in the era of multiple therapies: Biomarker set for risk stratification from a tertiary referral center;eLife;2023-05-30