Lessons Learned Using Real‐World Data to Emulate Randomized Trials: A Case Study of Treatment Effectiveness for Newly Diagnosed Immune Thrombocytopenia-Reference-Cited by-同舟云学术

Lessons Learned Using Real‐World Data to Emulate Randomized Trials: A Case Study of Treatment Effectiveness for Newly Diagnosed Immune Thrombocytopenia

Published:2021-09-15 Issue:6 Volume:110 Page:1570-1578
ISSN:0009-9236
Container-title:Clinical Pharmacology & Therapeutics
language:en
Short-container-title:Clin. Pharmacol. Ther.

Author:

McGrath Leah J.¹^ORCID,Nielson Carrie²,Saul Bradley¹,Breskin Alexander¹,Yu Ying¹,Nicolaisen Sia K.³,Kilpatrick Karynsa²,Ghanima Waleed⁴,Christiansen Christian F.³^ORCID,Bahmanyar Shahram⁵⁶,Linder Marie⁵,Eisen Melissa²,Wasser Jeffrey⁷,Altomare Ivy⁸,Kuter David⁹^ORCID,Sørensen Henrik T.³¹⁰,Kelsh Michael²,Brookhart M. Alan¹¹¹

Affiliation:

1. NoviSci, Inc Durham North Carolina USA

2. Center for Observational Research Amgen Thousand Oaks California USA

3. Department of Clinical Epidemiology Aarhus University Hospital Aarhus Denmark

4. Department of Hematology Institute of Clinical Medicine University of Oslo Oslo Norway

5. Clinical Epidemiology Division & Center for Pharmacoepidemiology Karolinska Institutet Stockholm Sweden

6. Centre for Psychiatry Research Karolinska Institutet Stockholm Sweden

7. University of Connecticut Farmington Connecticut USA

8. Flatiron Health Inc. New York New York USA

9. Department of Hematology Massachusetts General Hospital Boston Massachusetts USA

10. Department of Clinical Medicine Aarhus University Aarhus Denmark

11. Department of Population Health Sciences Duke University Durham North Carolina USA

Funder

Amgen

Publisher

Wiley

Subject

Pharmacology (medical),Pharmacology

Link

https://onlinelibrary.wiley.com/doi/pdf/10.1002/cpt.2399

Reference38 articles.

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4. Use of Real-world Data for New Drug Applications and Line Extensions

5. Bonamici S.H.R. 34 ‐ 21st Century Cures Act (2016). Accessed August 30 2021.

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