Bridging the Gap With Clinical Pharmacology in Innovative Rare Disease Treatment Modalities: Targeting DNA to RNA to Protein
Author:
Affiliation:
1. PTC Therapeutic, Inc. South Plainfield New Jersey USA
2. Lapix Therapeutics, Inc. Boston Massachusetts USA
Publisher
Wiley
Subject
Pharmacology (medical),Pharmacology
Link
https://onlinelibrary.wiley.com/doi/pdf/10.1002/jcph.2172
Reference74 articles.
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4. Important role of translational science in rare disease innovation, discovery, and drug development;Pariser AR;J Gen Intern Med,2014
5. Modeling and simulation in clinical pharmacology and dose finding;Staab A;CPT Pharmacometrics Syst Pharmacol,2013
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