Nusinersen improves walking distance and reduces fatigue in later‐onset spinal muscular atrophy-Reference-Cited by-同舟云学术

Nusinersen improves walking distance and reduces fatigue in later‐onset spinal muscular atrophy

Published:2019-07-27 Issue:4 Volume:60 Page:409-414
ISSN:0148-639X
Container-title:Muscle & Nerve
language:en
Short-container-title:Muscle Nerve

Author:

Montes Jacqueline¹²,Dunaway Young Sally³,Mazzone Elena S.⁴,Pasternak Amy⁵,Glanzman Allan M.⁶,Finkel Richard S.⁷,Darras Basil T.⁵,Muntoni Francesco⁸,Mercuri Eugenio⁴,De Vivo Darryl C.²⁹,Bishop Kathie M.¹⁰,Schneider Eugene¹⁰,Bennett C. Frank¹⁰,Foster Richard¹¹,Farwell Wildon¹²,

Affiliation:

1. Department of Rehabilitation and Regenerative MedicineColumbia University Irving Medical Center New York New York

2. Department of NeurologyColumbia University Irving Medical Center New York New York

3. Department of NeurologyStanford University School of Medicine Palo Alto California

4. Department of Paediatric NeurologyCatholic University Rome Italy

5. Department of NeurologyBoston Children's Hospital Boston Massachusetts

6. Department of Physical TherapyChildren's Hospital of Philadelphia Philadelphia Pennsylvania

7. Division of Neurology, Department of PediatricsNemours Children's Hospital Orlando Florida

8. Dubowitz Neuromuscular CentreUCL Great Ormond Street Institute of Child Health and NIHR Great Ormond Street Hospital Biomedical Research Centre London UK

9. Department PediatricsColumbia University Irving Medical Center New York New York

10. Clinical Development and Antisense ResearchIonis Pharmaceuticals, Inc Carlsbad California

11. Biostatistics, Biogen, Maidenhead UK

12. Clinical Development, Biogen Cambridge Massachusetts

Funder

Biogen

Publisher

Wiley

Subject

Physiology (medical),Cellular and Molecular Neuroscience,Neurology (clinical),Physiology

Link

https://onlinelibrary.wiley.com/doi/pdf/10.1002/mus.26633

Reference27 articles.

1. Identification and characterization of a spinal muscular atrophy-determining gene

2. Genetic Disorders Affecting the Motor Neuron

3. 209th ENMC International Workshop: Outcome Measures and Clinical Trial Readiness in Spinal Muscular Atrophy 7–9 November 2014, Heemskerk, The Netherlands

4. Spinal muscular atrophy

5. Ambulatory function in spinal muscular atrophy: Age-related patterns of progression

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