An updated systematic review on spinal muscular atrophy patients treated with nusinersen, onasemnogene abeparvovec (at least 24 months), risdiplam (at least 12 months) or combination therapies
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Elsevier BV
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1. Nusinersen Improves Motor Function in Type 2 and 3 Spinal Muscular Atrophy Patients across Time;Biomedicines;2024-08-06
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