Mir-142-3p target sequences reduce transgene-directed immunogenicity following intramuscular adeno-associated virus 1 vector-mediated gene delivery-Reference-Cited by-同舟云学术

Mir-142-3p target sequences reduce transgene-directed immunogenicity following intramuscular adeno-associated virus 1 vector-mediated gene delivery

Published:2013-06 Issue:6-7 Volume:15 Page:219-232
ISSN:1099-498X
Container-title:The Journal of Gene Medicine
language:en
Short-container-title:J Gene Med

Author:

Majowicz Anna,Maczuga Piotr,Kwikkers Karin L.¹,van der Marel Sander,van Logtenstein Richard¹,Petry Harald¹,van Deventer Sander J.,Konstantinova Pavlina¹,Ferreira Valerie¹

Affiliation:

1. Research and Development; uniQure BV; Amsterdam; The Netherlands

Publisher

Wiley

Subject

Genetics (clinical),Drug Discovery,Genetics,Molecular Biology,Molecular Medicine

Link

http://onlinelibrary.wiley.com/wol1/doi/10.1002/jgm.2712/fullpdf

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4. Peripheral transvenular delivery of adeno-associated viral vectors to skeletal muscle as a novel therapy for haemophilia B;Arruda;Blood,2010

5. AAV-mediated gene transfer in the perinatal period results in expression of FVII at levels that protect against fatal spontaneous haemorrhage;Binny;Blood,2012

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