Safety, pharmacodynamics, and potential benefit of omaveloxolone in Friedreich ataxia-Reference-Cited by-同舟云学术

Safety, pharmacodynamics, and potential benefit of omaveloxolone in Friedreich ataxia

Published:2018-11-10 Issue:1 Volume:6 Page:15-26
ISSN:2328-9503
Container-title:Annals of Clinical and Translational Neurology
language:en
Short-container-title:Ann Clin Transl Neurol

Author:

Lynch David R.¹,Farmer Jennifer²,Hauser Lauren¹,Blair Ian A.³,Wang Qing Qing³,Mesaros Clementina³,Snyder Nathaniel³,Boesch Sylvia⁴,Chin Melanie⁵,Delatycki Martin B.⁶,Giunti Paola⁷,Goldsberry Angela⁴,Hoyle Chad⁸,McBride Michael G.¹,Nachbauer Wolfgang⁴,O'Grady Megan⁵,Perlman Susan⁹,Subramony S. H.¹⁰,Wilmot George R.¹¹,Zesiewicz Theresa¹²,Meyer Colin⁵

Affiliation:

1. Division of Neurology; The Children's Hospital of Philadelphia; 502 Abramson Research Center 3615 Civic Center Blvd Philadelphia Pennsylvania 19104-4318

2. Friedreich's Ataxia Research Alliance; 533 W Uwchlan Ave Downingtown Pennsylvania 19335

3. Department of Systems Pharmacology and Translational Therapeutics; Perelman School of Medicine; University of Pennsylvania; Philadelphia Pennsylvania 19104

4. Department of Neurology; Medizinische Universität Innsbruck; Christoph-Probst-Platz 1 Innrain 52 6020 Innsbruck Austria

5. Reata Pharmaceuticals; 2801 Gateway Drive Suite 150 Irving Texas 75063

6. Victorian Clinical Genetics Services; Murdoch Children's Research Institute; Flemington Road Parkville Victoria 3052 Australia

7. Institute of Neurology University College of London; Queen Square London United Kingdom WC1N 3BG

8. Department of Neurology; The Ohio State University; 395 W. 12th Ave. 7th Floor Columbus Ohio 43210

9. Department of Neurology; University of California Los Angeles; BOX 956975 1-167 RNRC Los Angeles California 90095

10. Department of Neurology; McKnight Brain Institute; Room L3-100 1149 Newell Drive Gainesville Florida 32611

11. Department of Neurology; Emory University; 1365 Clifton Rd Atlanta Georgia 30322

12. Department of Neurology; University of South Florida; 12901 Bruce B Downs Blvd. MDC 55 Tampa Florida 33612

Funder

Reata Pharmaceutical

Publisher

Wiley

Subject

Neurology (clinical),General Neuroscience

Link

http://onlinelibrary.wiley.com/wol1/doi/10.1002/acn3.660/fullpdf

Reference36 articles.

1. Friedreich ataxia: effects of genetic understanding on clinical evaluation and therapy;Lynch;Arch Neurol,2002

2. Friedreich ataxia;Pandolfo;Arch Neurol,2008

3. Diagnosis and treatment of Friedreich ataxia: a European perspective;Schulz;Nat Rev Neurol,2009

4. Clinical features of Friedreich ataxia;Delatycki;J Child Neurol,2012

5. Progression of Friedreich ataxia: quantitative characterization over 5 years;Patel;Ann Clin Transl Neurol,2016

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