Endothelial Retargeting of AAV9 In Vivo-Reference-Cited by-同舟云学术

Endothelial Retargeting of AAV9 In Vivo

Published:2022-01-12 Issue:7 Volume:9 Page:2103867
ISSN:2198-3844
Container-title:Advanced Science
language:en
Short-container-title:Advanced Science

Author:

Bozoglu Tarik¹²,Lee Seungmin¹²,Ziegler Tilman¹²^ORCID,Jurisch Victoria¹²,Maas Sanne²³,Baehr Andrea¹²^ORCID,Hinkel Rabea¹²⁴^ORCID,Hoenig Amelie¹²,Hariharan Anjana¹²,Kim Christina Inyeop¹²,Decker Simon⁵,Sami Haider⁵,Koppara Tobias¹²,Oellinger Ruppert⁶,Müller Oliver J.⁷,Frank Derk⁷,Megens Remco³,Nelson Peter⁸,Weber Christian²³,Schnieke Angelika⁹,Sperandio Markus¹⁰,Santamaria Gianluca¹²,Rad Roland⁶,Moretti Alessandra¹²^ORCID,Laugwitz Karl‐Ludwig¹²,Soehnlein Oliver²³¹¹,Ogris Manfred⁵,Kupatt Christian¹²^ORCID

Affiliation:

1. Klinik und Poliklinik für Innere Medizin I University Clinic rechts der Isar Technical University Munich Germany

2. DZHK (German Center for Cardiovascular Research) Partner Site Munich Heart Alliance Munich Germany

3. Institute for Cardiovascular Prevention Ludwigs‐Maximilians‐University Munich Germany

4. Deutsches Primatenzentrum GmbH Leibnitz‐Institut für Primatenforschung Department of Laboratory Animal Science Göttingen Germany

5. Faculty of Life Sciences Department of Pharmaceutical Sciences Laboratory of MacroMolecular Cancer Therapeutics (MMCT) University of Vienna Althanstrasse 14 Vienna 1090 Austria

6. Institute of Molecular Oncology and Functional Genomics University Clinic rechts der Isar Technical University of Munic Germany

7. Klinik für Innere Medizin III and DZHK (German Center for Cardiovascular Research), partner site Hamburg, Kiel, Lübeck. UKSH Kiel Germany

8. Medizinische Klinik und Poliklinik IV Poliklinik Innenstadt Ludwigs‐Maximilians‐University Munich Germany

9. Department of Animal Sciences Chair of Livestock Biotechnology School of Life Sciences Weihenstephan Technical University Munich Germany

10. Walter Brendel Centre of Experimental Medicine and Institute of Cardiovascular Physiology and Pathophysiology BioMedical Centre Ludwig Maximilians University of Munich Germany

11. Institute for Experimental Pathology (ExPat) Center for Molecular Biology of Inflammation (ZMBE) WWU Münster Germany

Funder

European Research Council

Deutsche Forschungsgemeinschaft

Publisher

Wiley

Subject

General Physics and Astronomy,General Engineering,Biochemistry, Genetics and Molecular Biology (miscellaneous),General Materials Science,General Chemical Engineering,Medicine (miscellaneous)

Link

https://onlinelibrary.wiley.com/doi/pdf/10.1002/advs.202103867

Reference45 articles.

1. Hemophilia B Gene Therapy with a High-Specific-Activity Factor IX Variant

2. Recombinant AAV as a Platform for Translating the Therapeutic Potential of RNA Interference

3. Gene editing restores dystrophin expression in a canine model of Duchenne muscular dystrophy

4. Long-term evaluation of AAV-CRISPR genome editing for Duchenne muscular dystrophy

5. Somatic gene editing ameliorates skeletal and cardiac muscle failure in pig and human models of Duchenne muscular dystrophy

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