Promoterless, Nuclease‐Free Genome Editing Confers a Growth Advantage for Corrected Hepatocytes in Mice With Methylmalonic Acidemia-Reference-Cited by-同舟云学术

Promoterless, Nuclease‐Free Genome Editing Confers a Growth Advantage for Corrected Hepatocytes in Mice With Methylmalonic Acidemia

Published:2021-05-21 Issue:6 Volume:73 Page:2223-2237
ISSN:0270-9139
Container-title:Hepatology
language:en
Short-container-title:Hepatology

Author:

Chandler Randy J.¹,Venturoni Leah E.¹,Liao Jing²,Hubbard Brandon T.¹,Schneller Jessica L.¹,Hoffmann Victoria³,Gordo Susana²,Zang Shengwen²,Ko Chih‐Wei²,Chau Nelson²,Chiang Kyle²,Kay Mark A.⁴,Barzel Adi⁴⁵,Venditti Charles P.¹^ORCID

Affiliation:

1. National Human Genome Research InstituteNIH Bethesda MD

2. LogicBio Therapeutics Lexington MA

3. Office of Research Services NIH Bethesda MD

4. Departments of Pediatrics and Genetics Stanford University Stanford CA

5. Department of Biochemistry and Molecular Biology Tel Aviv University Tel Aviv Israel

Funder

National Heart, Lung, and Blood Institute

National Human Genome Research Institute

Publisher

Wiley

Subject