CRISPR-Cas9-mediated somatic correction of a one-base deletion in the Ugt1a gene ameliorates hyperbilirubinemia in Crigler-Najjar syndrome mice-Reference-Cited by-同舟云学术

CRISPR-Cas9-mediated somatic correction of a one-base deletion in the Ugt1a gene ameliorates hyperbilirubinemia in Crigler-Najjar syndrome mice

Published:2023-12 Issue: Volume:31 Page:101161
ISSN:2329-0501
Container-title:Molecular Therapy - Methods & Clinical Development
language:en
Short-container-title:Molecular Therapy - Methods & Clinical Development

Author:

Bortolussi Giulia,Iaconcig Alessandra,Canarutto Giulia,Porro Fabiola,Ferrucci Filippo,Galletta Claudia,Díaz-Muñoz Cristian,Rawat Vipin,De Caneva Alessia,Olajide Olayemi Joseph,Zentilin Lorena,Piazza Silvano,Bočkor Luka,Muro Andrés Fernando^ORCID

Funder

International Centre for Genetic Engineering and Biotechnology

Publisher

Elsevier BV

Subject

Genetics,Molecular Biology,Molecular Medicine

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5. Bilirubin-induced neurologic damage--mechanisms and management approaches;Watchko;N. Engl. J. Med.,2013

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