Bayesian methods to compare dose levels with placebo in a small n, sequential, multiple assignment, randomized trial
Author:
Affiliation:
1. Department of Biostatistics School of Public Health, University of Michigan Ann Arbor Michigan USA
2. Health Informatics Institute University of South Florida Tampa Florida USA
Funder
National Center for Advancing Translational Sciences
Patient-Centered Outcomes Research Institute
Publisher
Wiley
Subject
Statistics and Probability,Epidemiology
Link
https://onlinelibrary.wiley.com/doi/pdf/10.1002/sim.8813
Reference17 articles.
1. 107th Congress rare diseases act of 2002.Pub Law;2002:107‐280.
2. Clinical research for rare disease: Opportunities, challenges, and solutions
3. FDA guidance for industry (Draft). Rare diseases: common issues in drug development;2015.
4. Study design VII. Randomised controlled trials
5. A framework for applying unfamiliar trial designs in studies of rare diseases
Cited by 4 articles. 订阅此论文施引文献 订阅此论文施引文献,注册后可以免费订阅5篇论文的施引文献,订阅后可以查看论文全部施引文献
1. Dynamic Enrichment of Bayesian Small-Sample, Sequential, Multiple Assignment Randomized Trial Design Using Natural History Data: A Case Study from Duchenne Muscular Dystrophy;Biometrics;2023-06-15
2. Application of Bayesian approaches in drug development: starting a virtuous cycle;Nature Reviews Drug Discovery;2023-02-15
3. Comparing Dose Levels to Placebo using a Continuous Outcome in a Small n, Sequential, Multiple Assignment, Randomized trial (snSMART);Statistics in Biopharmaceutical Research;2022-10-07
4. Application of Bayesian methods to accelerate rare disease drug development: scopes and hurdles;Orphanet Journal of Rare Diseases;2022-05-07
1.学者识别学者识别
2.学术分析学术分析
3.人才评估人才评估
"同舟云学术"是以全球学者为主线,采集、加工和组织学术论文而形成的新型学术文献查询和分析系统,可以对全球学者进行文献检索和人才价值评估。用户可以通过关注某些学科领域的顶尖人物而持续追踪该领域的学科进展和研究前沿。经过近期的数据扩容,当前同舟云学术共收录了国内外主流学术期刊6万余种,收集的期刊论文及会议论文总量共计约1.5亿篇,并以每天添加12000余篇中外论文的速度递增。我们也可以为用户提供个性化、定制化的学者数据。欢迎来电咨询!咨询电话:010-8811{复制后删除}0370
www.globalauthorid.com
TOP
Copyright © 2019-2024 北京同舟云网络信息技术有限公司 京公网安备11010802033243号 京ICP备18003416号-3