Restoring ornithine transcarbamylase (OTC) activity in an OTC‐deficient mouse model using LUNAR‐OTC mRNA
Author:
Affiliation:
1. Arcturus Therapeutics San Diego California USA
2. Pyxant Labs Colorado Springs Colorado USA
3. Salvia Scientific Encinitas California USA
4. Miami University Oxford Ohio USA
5. Pharmaron Beijing Co. Beijing China
Publisher
Wiley
Link
https://onlinelibrary.wiley.com/doi/pdf/10.1002/ctd2.33
Reference9 articles.
1. Urea biosynthesis I. The urea cycle and relationships to the citric acid cycle
2. Long-term outcomes in Ornithine Transcarbamylase deficiency: a series of 90 patients
3. Neurological implications of urea cycle disorders
4. Abnormal ornithine carbamoyltransferase in mice having the sparse-fur mutation
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