Bayesian methods for the design and interpretation of clinical trials in very rare diseases-Reference-Cited by-同舟云学术

Bayesian methods for the design and interpretation of clinical trials in very rare diseases

Published:2014-06-23 Issue:24 Volume:33 Page:4186-4201
ISSN:0277-6715
Container-title:Statistics in Medicine
language:en
Short-container-title:Statist. Med.

Author:

Hampson Lisa V.¹,Whitehead John¹,Eleftheriou Despina²,Brogan Paul²

Affiliation:

1. Medical and Pharmaceutical Statistics Research Unit, Department of Mathematics and Statistics; Lancaster University; Lancaster, LA1 4YF U.K.

2. Department of Paediatric Rheumatology; UCL Institute of Child Health; 30 Guilford Street London WC1N 1EH U.K.

Funder

Medical Research Council

Arthritis Research UK

Publisher

Wiley

Subject

Statistics and Probability,Epidemiology

Link

http://onlinelibrary.wiley.com/wol1/doi/10.1002/sim.6225/fullpdf

Reference38 articles.

1. European Medicines Agency Guideline on clinical trials in small populations 2006 http://www.ema.europa.eu/docs/en_GB/document_library/Scientific_guideline/2009/09/WC500003615.pdf

2. Clinical trials and rare diseases: a way out of a conundrum;Lilford;British Medical Journal,1995

3. Small sample sizes in clinical trials: a statistician's perspective;Billingham;Clinical Investigation,2012

4. Summarizing historical information on controls in clinical trials;Neuenschwander;Clinical Trials 2010

5. The network meta-analytic-predictive approach to non-inferiority trials;Schmidli;Statistical Methods in Medical Research,2011

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