CRISPR correction of a homozygous low-density lipoprotein receptor mutation in familial hypercholesterolemia induced pluripotent stem cells

Author:

Omer Linda12ORCID,Hudson Elizabeth A.2,Zheng Shirong1,Hoying James B.13,Shan Yuan4,Boyd Nolan L.13

Affiliation:

1. Cardiovascular Innovation Institute; University of Louisville School of Medicine; Louisville KY

2. Department of Biochemistry and Molecular Genetics; University of Louisville School of Medicine; Louisville KY

3. Department of Physiology; University of Louisville School of Medicine; Louisville KY

4. Departments of Anatomic Pathology and Neurosurgery, Scott & White Medical Center, College of Medicine; Texas A&M University; Temple TX

Funder

National Institutes of Health

Jewish Heritage Fund for Excellence

Publisher

Wiley

Subject

General Medicine

Reference47 articles.

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