Enzyme replacement therapy with laronidase (Aldurazyme® ) for treating mucopolysaccharidosis type I-Reference-Cited by-同舟云学术

Enzyme replacement therapy with laronidase (Aldurazyme® ) for treating mucopolysaccharidosis type I

Published:2016-04-01 Issue: Volume: Page:
ISSN:1465-1858
Container-title:Cochrane Database of Systematic Reviews
language:en
Short-container-title:

Author:

Jameson Elisabeth¹,Jones Simon¹,Remmington Tracey²

Affiliation:

1. Central Manchester University Hospitals NHS Foundation Trust; Willink Biochemical Genetics Unit, Manchester Centre for Genomic Medicine; St Mary's Hospital Oxford Road Manchester UK M13 9WL

2. University of Liverpool; Department of Women's and Children's Health; Alder Hey Children's NHS Foundation Trust Eaton Road Liverpool UK L12 2AP

Publisher

Wiley

Subject

Pharmacology (medical)

Link

http://onlinelibrary.wiley.com/wol1/doi/10.1002/14651858.CD009354.pub4/fullpdf

Reference33 articles.

1. A phase 3 extension study of aldurazyme (laronidase) in mucopolysaccharidosis I (MPS I) [abstract];Clarke;Journal of Inherited Metabolic Disease,2006

2. Long-term efficacy and safety of laronidase in the treatment of mucopolysaccharidosis I;Clarke;Pediatrics,2009

3. Enzyme replacement therapy for mucopolysaccharidosis I: a randomized, double-blinded, placebo-controlled, multinational study of recombinant human alpha-L-iduronidase (laronidase);Wraith;Journal of Pediatrics,2004

4. Aldurazyme (laronidase) enzyme replacement therapy for MPS I: 96-week extension data [abstract];Wraith;Journal of Inherited Metabolic Disease,2005

5. A study of intrathecal enzyme replacement for cognitive decline in mucopolysaccharidosis I [abstract];Chen;Molecular Genetics and Metabolism,2015

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