1. Keck School of MedicineUniversity of Southern California/Children's Hospital Los Angeles Los Angeles California
2. Children's National Health System Washington District of Columbia
3. Division of Hematology‐OncologyBoston Children's Hospital/Harvard Medical School Boston Massachusetts
4. Carman and Ann Adams Department of PediatricsChildren's Hospital of Michigan/Wayne State University Detroit Michigan
5. Children's Minnesota Minneapolis Minnesota
6. Indiana Hemophilia and Thrombosis Center Indianapolis Indiana
7. Department of PediatricsChildren's Hospital Colorado Aurora Colorado
8. Cortica Healthcare San Diego California
9. Novo Nordisk Inc. Plainsboro New Jersey