Promoterless gene targeting without nucleases rescues lethality of a Crigler‐Najjar syndrome mouse model-Reference-Cited by-同舟云学术

Promoterless gene targeting without nucleases rescues lethality of a Crigler‐Najjar syndrome mouse model

Published:2017-07-27 Issue:10 Volume:9 Page:1346-1355
ISSN:1757-4676
Container-title:EMBO Molecular Medicine
language:en
Short-container-title:EMBO Mol Med

Author:

Porro Fabiola¹,Bortolussi Giulia¹,Barzel Adi²,De Caneva Alessia¹,Iaconcig Alessandra¹,Vodret Simone¹,Zentilin Lorena¹,Kay Mark A²,Muro Andrés F¹^ORCID

Affiliation:

1. International Centre for Genetic Engineering and Biotechnology (ICGEB) Trieste Italy

2. Departments of Pediatrics and Genetics Stanford University Stanford CA USA

Funder

National Institutes of Health

Publisher

EMBO

Subject

Molecular Medicine

Link

https://onlinelibrary.wiley.com/doi/pdf/10.15252/emmm.201707601

Reference49 articles.

1. Evolution of indications and results of liver transplantation in Europe. A report from the European Liver Transplant Registry (ELTR)

2. Robust ZFN-mediated genome editing in adult hemophilic mice

3. Quantitation of transplanted hepatic mass necessary to cure the gunn rat model of hyperbilirubinemia

4. Promoterless gene targeting without nucleases ameliorates haemophilia B in mice

5. Inverse zonation of hepatocyte transduction with AAV vectors between mice and non-human primates

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