Gene therapy for ADA‐SCID, the first marketing approval of an ex vivo gene therapy in Europe: paving the road for the next generation of advanced therapy medicinal products-Reference-Cited by-同舟云学术

Gene therapy for ADA‐SCID, the first marketing approval of an ex vivo gene therapy in Europe: paving the road for the next generation of advanced therapy medicinal products

Published:2017-04-10 Issue:6 Volume:9 Page:737-740
ISSN:1757-4676
Container-title:EMBO Molecular Medicine
language:en
Short-container-title:EMBO Mol Med

Author:

Aiuti Alessandro¹²^ORCID,Roncarolo Maria Grazia¹²,Naldini Luigi¹²

Affiliation:

1. San Raffaele Telethon Institute for Gene Therapy (SR‐Tiget) IRCCS San Raffaele Scientific Institute Milan Italy

2. Vita Salute San Raffaele University Milan Italy

Publisher

EMBO

Subject

Molecular Medicine

Link

https://onlinelibrary.wiley.com/doi/pdf/10.15252/emmm.201707573

Reference15 articles.

1. Correction of ADA-SCID by Stem Cell Gene Therapy Combined with Nonmyeloablative Conditioning

2. Multilineage hematopoietic reconstitution without clonal selection in ADA-SCID patients treated with stem cell gene therapy

3. Gene Therapy for Immunodeficiency Due to Adenosine Deaminase Deficiency

4. T Lymphocyte-Directed Gene Therapy for ADA − SCID: Initial Trial Results After 4 Years

5. Gene Therapy in Peripheral Blood Lymphocytes and Bone Marrow for ADA − Immunodeficient Patients

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