Prevalence of pyruvate kinase deficiency: A systematic literature review
Author:
Affiliation:
1. IQVIA Epidemiology & Drug Safety Cambridge MA USA
2. Agios Pharmaceuticals Inc. Cambridge MA USA
3. IQVIA Epidemiology & Drug Safety Seattle WA USA
Publisher
Wiley
Subject
Hematology,General Medicine
Link
https://onlinelibrary.wiley.com/doi/pdf/10.1111/ejh.13424
Reference47 articles.
1. PrchalJT.Pyruvate kinase deficiency.https://www.uptodate.com/contents/pyruvate‐kinase‐deficiency
2. Clinical spectrum of pyruvate kinase deficiency: data from the Pyruvate Kinase Deficiency Natural History Study
3. Genotype‐phenotype correlation and molecular heterogeneity in pyruvate kinase deficiency
4. Addressing the diagnostic gaps in pyruvate kinase deficiency: Consensus recommendations on the diagnosis of pyruvate kinase deficiency
5. Joanna Briggs Institute.Critical appraisal tools 2018.http://joannabriggs.org/research/critical‐appraisal‐tools.html
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