Mortality among US veterans with a physician-documented diagnosis of pyruvate kinase deficiency

Author:

Zagadailov Erin1,Al-Samkari Hanny2,Boscoe Audra N.3ORCID,McGee Bryan3,Shi Sherry4,Macaulay Dendy5,Shi Lizheng6,Garcia-Horton Viviana7

Affiliation:

1. Formerly of Agios Pharmaceuticals, Inc., Cambridge, MA, USA

2. Division of Hematology, Massachusetts General Hospital, Harvard Medical School, Boston, MA, USA

3. Agios Pharmaceuticals, Inc., Cambridge, MA, USA

4. Analysis Group, Inc., Montreal, Canada

5. Formerly Analysis Group, Inc., New York, NY, USA

6. School of Public Health & Tropical Medicine, Tulane University, New Orleans, LA, USA

7. Analysis Group, Inc., New York, NY, USA

Funder

Agios Pharmaceuticals, Inc

Publisher

Informa UK Limited

Subject

Hematology,Hematology

Reference31 articles.

1. A specific erythrocyte glycolytic enzyme defect (pyruvate kinase) in three subjects with congenital non-spherocytic hemolytic anemia;Valentine WN;Trans Assoc Am Phys,1961

2. Pyruvate Kinase (PK) Deficiency Hereditary Nonspherocytic Hemolytic Anemia

3. Management of pyruvate kinase deficiency in children and adults

4. Prevalence of pyruvate kinase deficiency: A systematic literature review

5. Molecular heterogeneity of pyruvate kinase deficiency

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