Gene therapy for immune tolerance induction in hemophilia with inhibitors
Author:
Affiliation:
1. The Children's Hospital of Philadelphia; Philadelphia PA USA
2. Perelman Center for Cell and Molecular Therapeutics; Philadelphia PA USA
3. Perelman School of Medicine at the University of Pennsylvania; Philadelphia PA USA
Funder
Novo Nordisk Inc
Publisher
Wiley
Subject
Hematology
Link
http://onlinelibrary.wiley.com/wol1/doi/10.1111/jth.13331/fullpdf
Reference99 articles.
1. International workshop on immune tolerance induction: consensus recommendations;DiMichele;Haemophilia,2007
2. Toward optimal therapy for inhibitors in hemophilia;Kempton;Blood,2014
3. Inhibitor development in haemophilia B: an orphan disease in need of attention;DiMichele;Br J Haematol,2007
4. Impact of inhibitors on hemophilia A mortality in the United States;Walsh;Am J Hematol,2015
5. Inhibitor development and mortality in non-severe hemophilia A;Eckhardt;J Thromb Haemost,2015
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