Intrathecal baclofen in metachromatic leukodystrophy-Reference-Cited by-同舟云学术

Intrathecal baclofen in metachromatic leukodystrophy

Published:2018-05-27 Issue:2 Volume:61 Page:232-235
ISSN:0012-1622
Container-title:Developmental Medicine & Child Neurology
language:en
Short-container-title:Dev Med Child Neurol

Author:

van der Veldt Nikki¹^ORCID,van Rappard Diane F²,van de Pol Laura A²,van der Knaap Marjo S²,van Ouwerkerk Willem J R³,Becher Jules G¹,Wolf Nicole I²,Buizer Annemieke I¹^ORCID

Affiliation:

1. Department of Rehabilitation Medicine; VU University Medical Center; Amsterdam Movement Sciences; Amsterdam the Netherlands

2. Department of Child Neurology; Center for Childhood White Matter Disorders; VU University Medical Center and Amsterdam Neuroscience; Amsterdam the Netherlands

3. Department of Neurosurgery; VU University Medical Center; Amsterdam the Netherlands

Publisher

Wiley

Subject

Neurology (clinical),Developmental Neuroscience,Pediatrics, Perinatology and Child Health

Link

http://onlinelibrary.wiley.com/wol1/doi/10.1111/dmcn.13919/fullpdf

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3. Metachromatic leukodystrophy: disease spectrum and approaches for treatment;Rappard;Best Pract Res Clin Endocrinol Metab,2015

4. Efficacy of hematopoietic cell transplantation in metachromatic leukodystrophy: the Dutch experience;Rappard;Blood,2016

5. Lentiviral haemopoietic stem-cell gene therapy in early-onset metachromatic leukodystrophy: an ad-hoc analysis of a non-randomised, open-label, phase 1/2 trial;Sessa;Lancet,2016

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