Metachromatic leukodystrophy: an overview of current and prospective treatments
Author:
Publisher
Springer Science and Business Media LLC
Subject
Transplantation,Hematology
Link
http://www.nature.com/articles/bmt2008275.pdf
Reference45 articles.
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4. Souillet G, Guffon N, Maire I, Pujol M, Taylor P, Sevin F et al. Outcome of 27 patients with Hurler's syndrome transplanted from either related or unrelated haematopoietic stem cell sources. Bone marrow Transplant 2003; 31: 1105–1117.
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