1. US Food and Drug Administration, FDA approves first-of-its kind targeted RNA-based therapy to treat a rare disease, 2018. https://www.fda.gov/news-events/press-announcements/fda-approves-first-its-kind-targeted-rna-based-therapy-treat-rare-disease.
2. C.A. Bradley, First antisense drug is approved with fleeting success, 2019. https://www.nature.com/articles/d42859-019-00080-6.
3. Antisense oligonucleotides as potential therapeutics for type 2 diabetes;Chen;Nucleic Acid Ther.,2020
4. Patisiran for the treatment of hereditary transthyretin-mediated amyloidosis;Yang;Expert Rev. Clin. Pharmacol.,2019
5. US Food and Drug Administration, FDA Approves First Drug to Treat Rare Metabolic Disorder, 2020. https://www.fda.gov/news-events/press-announcements/fda-approves-first-drug-treat-rare-metabolic-disorder.