Characterization of an immunodeficient mouse model of mucopolysaccharidosis type I suitable for preclinical testing of human stem cell and gene therapy
Author:
Publisher
Elsevier BV
Subject
General Neuroscience
Reference38 articles.
1. A newly discovered class of human hematopoietic cells with SCID-repopulating activity;Bhatia;Nat. Med.,1998
2. A rapid and sensitive method for the quantitation of microgram quantities of protein utilizing the principle of protein-dye binding;Bradford;Anal. Biochem.,1976
3. Cardiac functional and histopathologic findings in humans and mice with mucopolysaccharidosis type I: implications for assessment of therapeutic interventions in hurler syndrome;Braunlin;Pediatr. Res.,2006
4. Microdetermination of proteoglycans and glycosaminglycans in the presence of guanidine hydrochloride;Chandrasekhar;Anal. Biochem.,1987
5. Murine mucopolysaccharidosis type I: targeted disruption of the murine alpha-l-iduronidase gene;Clarke;Hum. Mol. Genet.,1997
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