Long term clinical effectiveness of ivacaftor in people with the G551D CFTR mutation
Author:
Funder
Cystic Fibrosis Foundation Therapeutics
National Institutes of Health
Publisher
Elsevier BV
Subject
Pulmonary and Respiratory Medicine,Pediatrics, Perinatology and Child Health
Reference38 articles.
1. Effect of VX-770 in persons with cystic fibrosis and the G551D-CFTR mutation;Accurso;N Engl J Med,2010
2. A CFTR potentiator in patients with cystic fibrosis and the G551D mutation;Ramsey;N Engl J Med,2011
3. Rescue of CF airway epithelial cell function in vitro by a CFTR potentiator, VX-770;Van Goor,2009
4. Clinical mechanism of the cystic fibrosis transmembrane conductance regulator potentiator ivacaftor in G551D-mediated cystic fibrosis;Rowe;Am. J. Respir. Crit. Care Med.,2014
5. Impact of CFTR modulation on intestinal pH, motility, and clinical outcomes in patients with cystic fibrosis and the G551D mutation;Gelfond;Clin Transl Gastroenterol,2017
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