Once-daily, subcutaneous vosoritide therapy in children with achondroplasia: a randomised, double-blind, phase 3, placebo-controlled, multicentre trial-Reference-Cited by-同舟云学术

Once-daily, subcutaneous vosoritide therapy in children with achondroplasia: a randomised, double-blind, phase 3, placebo-controlled, multicentre trial

Published:2020-09 Issue:10252 Volume:396 Page:684-692
ISSN:0140-6736
Container-title:The Lancet
language:en
Short-container-title:The Lancet

Author:

Savarirayan Ravi,Tofts Louise,Irving Melita,Wilcox William,Bacino Carlos A,Hoover-Fong Julie,Ullot Font Rosendo,Harmatz Paul,Rutsch Frank,Bober Michael B,Polgreen Lynda E,Ginebreda Ignacio,Mohnike Klaus,Charrow Joel,Hoernschemeyer Daniel,Ozono Keiichi,Alanay Yasemin,Arundel Paul,Kagami Shoji,Yasui Natsuo,White Klane K,Saal Howard M,Leiva-Gea Antonio,Luna-González Felipe,Mochizuki Hiroshi,Basel Donald,Porco Dania M,Jayaram Kala,Fisheleva Elena,Huntsman-Labed Alice,Day Jonathan

Funder

BioMarin Pharmaceutical

Shire

Publisher

Elsevier BV

Subject

General Medicine

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