Twelve years of experience with miglustat in the treatment of type 1 Gaucher disease: The Spanish ZAGAL project-Reference-Cited by-同舟云学术

Twelve years of experience with miglustat in the treatment of type 1 Gaucher disease: The Spanish ZAGAL project

Published:2018-02 Issue: Volume:68 Page:173-179
ISSN:1079-9796
Container-title:Blood Cells, Molecules, and Diseases
language:en
Short-container-title:Blood Cells, Molecules, and Diseases

Author:

Giraldo Pilar,Andrade-Campos Marcio,Alfonso Pilar,Irun Pilar,Atutxa Koldo,Acedo Antonio,Barez Abelardo,Blanes Margarita,Diaz-Morant Vicente,Fernández-Galán Ma Angeles,Franco Rafael,Gil-Cortes Cristina,Giner Vicente^ORCID,Ibañez Angela,Latre Paz,Loyola Ines,Luño Elisa^ORCID,Hernández-Martin Roberto,Medrano-Engay Blanca,Puerta José,Roig Inmaculada,de la Serna Javier^ORCID,Salamero Olga,Villalón Lucia,Pocovi Miguel

Funder

FEETEG

Actelion Pharmaceuticals Ltd

Publisher

Elsevier BV

Subject

Cell Biology,Hematology,Molecular Biology,Molecular Medicine

Reference36 articles.

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4. Low-dose enzyme replacement therapy for Gaucher's disease: effects of age, sex, genotype, and clinical features on response to treatment;Zimran;Am. J. Med.,1994

5. The long-term international safety experience of imiglucerase therapy for Gaucher disease;Starzyk;Mol. Genet. Metab.,2007

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