Low-dose enzyme replacement therapy for Gaucher's disease: Effects of age, sex, genotype, and clinical features on response to treatment
Author:
Publisher
Elsevier BV
Subject
General Medicine
Reference29 articles.
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4. Enzyme augmentation in moderate to life threatening Gaucher disease;Fallet;Pediatr Res,1992
5. Successful treatment of bone marrow failure in Gaucher's disease with low dose modified glucocerebrosidase;Mistry;Q J Med,1992
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