Long-term efficacy and safety results of taliglucerase alfa through 5 years in adult treatment-naïve patients with Gaucher disease-Reference-Cited by-同舟云学术

Long-term efficacy and safety results of taliglucerase alfa through 5 years in adult treatment-naïve patients with Gaucher disease

Published:2019-09 Issue: Volume:78 Page:14-21
ISSN:1079-9796
Container-title:Blood Cells, Molecules, and Diseases
language:en
Short-container-title:Blood Cells, Molecules, and Diseases

Author:

Zimran Ari,Durán Gloria,Giraldo Pilar,Rosenbaum Hanna,Giona Fiorina,Petakov Milan,Terreros Muñoz Eduardo,Solorio-Meza Sergio Eduardo,Cooper Peter A.,Varughese Sheeba,Alon Sari,Chertkoff Raul

Funder

Protalix BioTherapeutics

Publisher

Elsevier BV

Subject

Cell Biology,Hematology,Molecular Biology,Molecular Medicine

Reference15 articles.

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5. Replacement therapy for inherited enzyme deficiency–macrophage-targeted glucocerebrosidase for Gaucher's disease;Barton;N. Engl. J. Med.,1991

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