Nonsense codons suppression. An acute toxicity study of three optimized TRIDs in murine model, safety and tolerability evaluation

Author:

Corrao Federica,Zizzo Maria Grazia,Tutone Marco,Melfi Raffaella,Fiduccia Ignazio,Carollo Pietro Salvatore,Leonardo Aldo Di,Caldara Gaetano,Perriera Riccardo,Pace Andrea,Belmonte Beatrice,Sammataro Selene,Pibiri Ivana,Lentini LauraORCID

Publisher

Elsevier BV

Subject

Pharmacology,General Medicine

Reference31 articles.

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3. Chapter 2 – Pathologies Susceptible to be Targeted for Nonsense Mutation Therapies. Nonsense Mutation Correction in Human Diseases. An Approach for Targeted Medicine 2016;Benhabiles,2016

4. Novel translational read-through-inducing drugs as a therapeutic option for shwachman-diamond syndrome;Bezzerri;Biomedicines,2022

5. A comprehensive analysis of choroideremia: from genetic characterization to clinical practice;Sanchez-Alcudia;PLoS One,2016

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