Lung gene therapy—How to capture illumination from the light already present in the tunnel
Author:
Funder
Canadian Institutes of Health Research
Publisher
Elsevier BV
Subject
Cell Biology,Genetics(clinical),Molecular Biology,Biochemistry
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3. Human gene therapy for RPE65 isomerase deficiency activates the retinoid cycle of vision but with slow rod kinetics;Cideciyan;Proc Natl Acad Sci U S A,2008
4. Leber congenital amaurosis: comprehensive survey of the genetic heterogeneity, refinement of the clinical definition, and genotype-phenotype correlations as a strategy for molecular diagnosis;Hanein;Hum Mutat,2004
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