TALEN-mediated functional correction of X-linked chronic granulomatous disease in patient-derived induced pluripotent stem cells
Author:
Publisher
Elsevier BV
Subject
Mechanics of Materials,Biomaterials,Biophysics,Ceramics and Composites,Bioengineering
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3. Correction of X-linked chronic granulomatous disease by gene therapy, augmented by insertional activation of MDS1-EVI1, PRDM16 or SETBP1;Ott;Nat. Med.,2006
4. Genomic instability and myelodysplasia with monosomy 7 consequent to EVI1 activation after gene therapy for chronic granulomatous disease;Stein;Nat. Med.,2010
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