Dose-Dependent Prevention of Metabolic and Neurologic Disease in Murine MPS II by ZFN-Mediated In Vivo Genome Editing-Reference-Cited by-同舟云学术

Dose-Dependent Prevention of Metabolic and Neurologic Disease in Murine MPS II by ZFN-Mediated In Vivo Genome Editing

Published:2018-04 Issue:4 Volume:26 Page:1127-1136
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Laoharawee Kanut,DeKelver Russell C.,Podetz-Pedersen Kelly M.,Rohde Michelle,Sproul Scott,Nguyen Hoang-Oanh,Nguyen Tam,St. Martin Susan J.,Ou Li,Tom Susan,Radeke Robert,Meyer Kathleen E.,Holmes Michael C.,Whitley Chester B.,Wechsler Thomas,McIvor R. Scott

Funder

Sangamo Therapeutics

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

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