Non-viral Delivery of Zinc Finger Nuclease mRNA Enables Highly Efficient In Vivo Genome Editing of Multiple Therapeutic Gene Targets-Reference-Cited by-同舟云学术

Non-viral Delivery of Zinc Finger Nuclease mRNA Enables Highly Efficient In Vivo Genome Editing of Multiple Therapeutic Gene Targets

Published:2019-04 Issue:4 Volume:27 Page:866-877
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Conway Anthony,Mendel Matthew,Kim Kenneth,McGovern Kyle,Boyko Alisa,Zhang Lei,Miller Jeffrey C.,DeKelver Russell C.,Paschon David E.,Mui Barbara L.,Lin Paulo J.C.,Tam Ying K.,Barbosa Chris,Redelmeier Tom,Holmes Michael C.,Lee Gary

Funder

Sangamo Therapeutics

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

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4. Correction of a genetic disease in mouse via use of CRISPR-Cas9;Wu;Cell Stem Cell,2013

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