Ex Vivo Selection of Transduced Hematopoietic Stem Cells for Gene Therapy of β-Hemoglobinopathies-Reference-Cited by-同舟云学术

Ex Vivo Selection of Transduced Hematopoietic Stem Cells for Gene Therapy of β-Hemoglobinopathies

Published:2018-02 Issue:2 Volume:26 Page:480-495
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Bhukhai Kanit,de Dreuzy Edouard,Giorgi Marie,Colomb Charlotte,Negre Olivier,Denaro Maria,Gillet-Legrand Béatrix,Cheuzeville Joëlle,Paulard Anaïs,Trebeden-Negre Hélène,Borwornpinyo Suparerk,Sii-Felice Karine,Maouche Leila,Down Julian D.,Leboulch Phillippe,Payen Emmanuel

Funder

“Agence Nationale pour la Recherche”

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

Reference67 articles.

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3. Advances in stem cell transplantation and gene therapy in the beta-hemoglobinopathies;Payen;Hematology Am. Soc. Hematol. Educ. Program,2012

4. Update from the Hgb-205 phase 1/2 clinical study of lentiglobin gene therapy: sustained clinical benefit in severe hemoglobinopathies;Ribeil;Blood,2016

5. Gene therapy in a patient with sickle cell disease;Ribeil;N. Engl. J. Med.,2017

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