Gene Therapy of the β-Hemoglobinopathies by Lentiviral Transfer of the βA(T87Q)-GlobinGene-Reference-Cited by-同舟云学术

Gene Therapy of the β-Hemoglobinopathies by Lentiviral Transfer of the βA(T87Q)-GlobinGene

Published:2016-02 Issue:2 Volume:27 Page:148-165
ISSN:1043-0342
Container-title:Human Gene Therapy
language:en
Short-container-title:Human Gene Therapy

Author:

Negre Olivier¹²,Eggimann Anne-Virginie¹,Beuzard Yves²³,Ribeil Jean-Antoine⁴,Bourget Philippe⁴,Borwornpinyo Suparerk⁵,Hongeng Suradej⁵,Hacein-Bey Salima⁶,Cavazzana Marina⁴,Leboulch Philippe²³⁵⁷,Payen Emmanuel²³⁸

Affiliation:

1. bluebird bio, Cambridge, Massachusetts.

2. CEA, Institute of Emerging Disease and Innovative Therapies (iMETI), Fontenay aux Roses, France.

3. UMR 007, University of Paris 11 and CEA, CEA-iMETI, Fontenay aux Roses, France.

4. Necker Hospital, Assistance Publique-Hôpitaux de Paris, Paris, France.

5. Mahidol University, Bangkok, Thailand.

6. Immunology Laboratory, Groupe Hospitalier Universitaire Paris-Sud, Assistance Publique–Hôpitaux de Paris, Paris, France.

7. Harvard Medical School and Genetics Division, Department of Medicine, Brigham & Women's Hospital, Boston, Massachusetts.

8. INSERM, Paris, France.

Publisher

Mary Ann Liebert Inc

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

http://www.liebertpub.com/doi/pdf/10.1089/hum.2016.007

Reference153 articles.

1. Global epidemiology of haemoglobin disorders and derived service indicators

2. Global epidemiology of sickle haemoglobin in neonates: a contemporary geostatistical model-based map and population estimates

3. The genetic control of protein synthesis: The haemoglobin model

4. Improved survival of thalassaemia major in the UK and relation to T2* cardiovascular magnetic resonance

5. Mortality In Sickle Cell Disease -- Life Expectancy and Risk Factors for Early Death

Cited by 132 articles. 订阅此论文施引文献订阅此论文施引文献，注册后可以免费订阅5篇论文的施引文献，订阅后可以查看论文全部施引文献

1. Gene-addition/editing therapy in sickle cell disease;La Presse Médicale;2023-12

2. Applying the CRISPR/Cas9 for Treating Human and Animal Diseases – Comprehensive Review;Annals of Animal Science;2023-11-01

3. Sickle Cell Disease: From Genetics to Curative Approaches;Annual Review of Genomics and Human Genetics;2023-08-25

4. Defining global strategies to improve outcomes in sickle cell disease: a Lancet Haematology Commission;The Lancet Haematology;2023-08

5. A mass spectrometry assay for detection of endogenous and lentiviral engineered hemoglobin in cultured cells and sickle cell disease mice;The Journal of Gene Medicine;2023-07-17