ZFN-Mediated In Vivo Genome Editing Corrects Murine Hurler Syndrome-Reference-Cited by-同舟云学术

ZFN-Mediated In Vivo Genome Editing Corrects Murine Hurler Syndrome

Published:2019-01 Issue:1 Volume:27 Page:178-187
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Ou Li,DeKelver Russell C.,Rohde Michelle,Tom Susan,Radeke Robert,St. Martin Susan J.,Santiago Yolanda,Sproul Scott,Przybilla Michelle J.,Koniar Brenda L.,Podetz-Pedersen Kelly M.,Laoharawee Kanut,Cooksley Renee D.,Meyer Kathleen E.,Holmes Michael C.,McIvor R. Scott,Wechsler Thomas,Whitley Chester B.

Funder

Sangamo Therapeutics

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

Reference36 articles.

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