AAV-Mediated expression of galactocerebrosidase in brain results in attenuated symptoms and extended life span in murine models of globoid cell leukodystrophy-Reference-Cited by-同舟云学术

AAV-Mediated expression of galactocerebrosidase in brain results in attenuated symptoms and extended life span in murine models of globoid cell leukodystrophy

Published:2005-05 Issue:5 Volume:11 Page:734-744
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Rafi Mohammad A.,Zhi Rao Han,Passini Marco A.,Curtis Mark,Vanier Marie T.,Zaka Mariam,Luzi Paola,Wolfe John H.,Wenger David A.

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

Reference52 articles.

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5. Twenty-five years of the “psychosine hypothesis”: a personal perspective of its history and present status;Suzuki;Neurochem. Res.,1998

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