Preclinical studies in Krabbe disease: A model for the investigation of novel combination therapies for lysosomal storage diseases-Reference-Cited by-同舟云学术

登录注册会员服务联系我们

Preclinical studies in Krabbe disease: A model for the investigation of novel combination therapies for lysosomal storage diseases

Published:2023-01 Issue:1 Volume:31 Page:7-23
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Heller Gregory,Bradbury Allison M.,Sands Mark S.,Bongarzone Ernesto R.^ORCID

Funder

NINDS

Israel National Road Safety Authority

Eunice Kennedy Shriver National Institute of Child Health and Human Development

Legacy of Angels Foundation

Association Européenne contre les Leucodystrophies

National Institutes of Health

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

Reference207 articles.

1. CNS-targeting therapies for lysosomal storage diseases: current advances and challenges;Edelmann;Front. Mol. Biosci.,2020

2. Infantile form of diffuse brain-sclerosis;Krabbe;Brain,1916

3. Diagnosis of Krabbe's infantile leucodystrophy;Hagberg;J. Neurol. Neurosurg. Psychiatry,1963

4. Hospitalization burden and incidence of krabbe disease;Ghabash;J. Child Neurol.,2022

5. Newborn screening for Krabbe disease in New York State: the first eight years' experience;Orsini;Genet. Med.,2016

Cited by 8 articles. 订阅此论文施引文献订阅此论文施引文献，注册后可以免费订阅5篇论文的施引文献，订阅后可以查看论文全部施引文献

1. Human iPSC-derived myelinating organoids and globoid cells to study Krabbe Disease;2024-07-23

2. From pathological mechanisms in Krabbe disease to cutting‐edge therapy: A comprehensive review;Neuropathology;2024-03-06

3. Progress in leukodystrophies with zebrafish;Development, Growth & Differentiation;2024-01

4. Combination HSCT and intravenous AAV-mediated gene therapy in a canine model proves pivotal for translation of Krabbe disease therapy;Molecular Therapy;2024-01

5. HDAC-6 inhibition ameliorates the early neuropathology in a mouse model of Krabbe disease;Frontiers in Molecular Neuroscience;2023-07-27

同舟云学术

1.学者识别学者识别

2.学术分析学术分析

3.人才评估人才评估

"同舟云学术"是以全球学者为主线，采集、加工和组织学术论文而形成的新型学术文献查询和分析系统，可以对全球学者进行文献检索和人才价值评估。用户可以通过关注某些学科领域的顶尖人物而持续追踪该领域的学科进展和研究前沿。经过近期的数据扩容，当前同舟云学术共收录了国内外主流学术期刊6万余种，收集的期刊论文及会议论文总量共计约1.5亿篇，并以每天添加12000余篇中外论文的速度递增。我们也可以为用户提供个性化、定制化的学者数据。欢迎来电咨询！咨询电话：010-8811{复制后删除}0370

www.globalauthorid.com

TOP

Copyright © 2019-2024 北京同舟云网络信息技术有限公司
京公网安备11010802033243号京ICP备18003416号-3