In vivo adenine base editing rescues adrenoleukodystrophy in a humanized mouse model
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Published:2024-07
Issue:7
Volume:32
Page:2190-2206
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ISSN:1525-0016
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Container-title:Molecular Therapy
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language:en
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Short-container-title:Molecular Therapy
Author:
Gopalappa Ramu,
Lee MinYoungORCID,
Kim Globinna,
Jung Eul Sik,
Lee Hanahrae,
Hwang Hye-Yeon,
Lee Jong Geol,
Kim Su Jung,
Yoo Hyun Ju,
Sung Young Hoon,
Kim Daesik,
Baek In-Jeoung,
Kim Hyongbum HenryORCID
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