Safety and efficacy of leriglitazone for preventing disease progression in men with adrenomyeloneuropathy (ADVANCE): a randomised, double-blind, multi-centre, placebo-controlled phase 2

Safety and efficacy of leriglitazone for preventing disease progression in men with adrenomyeloneuropathy (ADVANCE): a randomised, double-blind, multi-centre, placebo-controlled phase 2–3 trial

Published:2023-02 Issue:2 Volume:22 Page:127-136
ISSN:1474-4422
Container-title:The Lancet Neurology
language:en
Short-container-title:The Lancet Neurology

Author:

Köhler Wolfgang,Engelen Marc,Eichler Florian,Lachmann Robin,Fatemi Ali,Sampson Jacinda,Salsano Ettore,Gamez Josep,Molnar Maria Judit,Pascual Sílvia,Rovira Maria,Vilà Anna,Pina Guillem,Martín-Ugarte Itziar,Mantilla Adriana,Pizcueta Pilar,Rodríguez-Pascau Laura,Traver Estefania,Vilalta Anna,Pascual María,Martinell Marc,Meya Uwe,Mochel Fanny,Mc Govern Eavan,Yazbeck Elise,Barbier Magali,Luton Marie-Pierre,Pousset Françoise,Hogrel Jean-Yves,Adanyeguh Isaac,Then Bergh Florian,Bergner Caroline,Unterlauft Astrid,Roicke Hannes,Hoffmann Karl-Titus,Scherlach Cordula,Kalb Andrea,Meilick Bianca,Reuschel Mandy,Fenu Silvia,Mauro Elena,Murphy Elaine,Krishna Gauri,Beyene Tiggy,Sierra Alba,Quiñoa Sara,Belen Canovas Anna,Grosz Zoltan,Györgyi Báthori,van de Stadt S.I.,Huffnagel I.C.,van Ballegoij W.J.C.,Voermans M.M.C.,Seyedsadjadi Reza,Corre Camille,Godbole Neha,Grant Natalie Rose,Brito Pires Claudia Maria,Trovato Melissa,Yeh Nancy,Goodman Jordan,Keller Jennifer,Joseph Chris,Van Haren Keith,Sakamuri Sarada,Duong Tina,Perrone Lila,Tran Stephanie,Dunaway Young Sally,Hashmi Syed

Publisher

Elsevier BV

Subject

Neurology (clinical)

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4. Postural body sway as surrogate outcome for myelopathy in adrenoleukodystrophy;van Ballegoij;Front Physiol,2020

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