Encouraging and Unsettling Findings in Long-Term Follow-up of AAV Gene Transfer
Author:
Publisher
Elsevier BV
Subject
Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine
Reference6 articles.
1. Efficacy, Safety, and Durability of Voretigene Neparvovec-rzyl in RPE65 Mutation-Associated Inherited Retinal Dystrophy: Results of Phase 1 and 3 Trials;Maguire;Ophthalmology,2019
2. Liver Gene Therapy: Reliable and Durable?;Herzog;Mol. Ther.,2019
3. Multiyear Follow-up of AAV5-hFVIII-SQ Gene Therapy for Hemophilia A;Pasi;N. Engl. J. Med.,2020
4. 5 Year Expression and Neutrophil Defect Repair after Gene Therapy in Alpha-1 Antitrypsin Deficiency;Mueller;Mol. Ther.,2017
5. Muscle-directed delivery of an AAV1 vector leads to capsid specific T cell exhaustion in nonhuman primates and humans;Gernoux;Mol. Ther.,2020
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